Biopharmaceutical company developing rare-disease treatments with three FDA-approved drugs
Mirum is a public biopharmaceutical company operating across clinical development, regulatory affairs, and commercial execution for rare liver and metabolic diseases. The tech stack is compliance-heavy (Veeva QMS, CDISC, SAS, Electronic Data Capture) and sales-infrastructure-focused (Salesforce, Adaptive Planning, Power BI), reflecting a tightly regulated environment where data integrity and audit readiness drive tooling choices. Active hiring across medical affairs, clinical, and finance—with director-level roles accelerating—signals scaling of evidence generation and regulatory operations alongside commercial growth.
Notable leadership hires: Global Medical Affairs Lead, Brand Lead, IT Integration Lead, CRM Lead, FP&A Director
Mirum Pharmaceuticals develops and commercializes medications for rare diseases. The company portfolio includes three FDA-approved drugs: LIVMARLI (an IBAT inhibitor for cholestatic pruritus in Alagille syndrome and PFIC), CHOLBAM (cholic acid for bile acid synthesis disorders and peroxisomal disorders), and CTEXLI (chenodiol for cerebrotendinous xanthomatosis). The pipeline includes late-stage investigational therapies for primary sclerosing cholangitis and other rare cholestatic conditions. Based in Foster City, California, Mirum operates across the United States, Germany, and Switzerland with 201–500 employees. The organization balances clinical development, regulatory strategy, and commercial execution for a patient population spanning pediatric and adult rare-disease indications.
Mirum's primary tools include Veeva (QMS and CRM), Salesforce, SAS, Electronic Data Capture, CDISC standards, Adaptive Planning, Power BI, Tableau, and Microsoft cloud services (Azure AD, Microsoft 365, Teams, OneDrive, SharePoint). The stack emphasizes regulatory compliance, data standardization, and commercial analytics.
Mirum has three approved medications: LIVMARLI (maralixibat) for cholestatic pruritus in Alagille syndrome and PFIC; CHOLBAM (cholic acid) for bile acid synthesis disorders and peroxisomal disorders; and CTEXLI (chenodiol) for cerebrotendinous xanthomatosis in adults.
Other companies in the same industry, closest in size