Biopharmaceutical company commercializing rare-disease treatments across three approved medicines
Mirum is a public biopharmaceutical company with three FDA-approved medications for rare liver and metabolic diseases, now scaling commercial and regulatory operations. The hiring acceleration—36 roles posted in the last 30 days across sales, healthcare, and market access—reflects active label-expansion studies (EXPAND for LIVMARLI) and pipeline advancement. The tech stack is clinical-stage heavy (Veeva QMS, Electronic Data Capture, LC-MS/MS, CDISC, SAS) paired with commercial tools (Salesforce, Veeva), signaling simultaneous focus on manufacturing compliance and revenue growth.
Notable leadership hires: IT Integration Lead, Market Access Director, FP&A Director, Sales Director, Associate Director, Publications
Mirum Pharmaceuticals develops treatments for rare childhood and adult diseases affecting the liver, bile acid metabolism, and lipid storage. The company has commercialized three medicines: LIVMARLI (an IBAT inhibitor for cholestatic pruritus in Alagille syndrome and PFIC), CHOLBAM (cholic acid for bile acid synthesis disorders), and CTEXLI (chenodiol for cerebrotendinous xanthomatosis). Mirum is advancing late-stage pipeline programs, including Phase 3 label-expansion work and Phase 2b studies in primary sclerosing cholangitis. Operations span the U.S. and Switzerland, with documented pain points in regulatory timing, rare-disease patient diagnosis rates, and global supply-chain coordination.
Mirum uses Veeva (QMS, Vault), SAS, CDISC, LC-MS/MS, Electronic Data Capture, and Komodo for clinical/manufacturing operations. Commercial systems include Salesforce, DocuSign, Power BI, Tableau, and Adaptive Planning. Identity and collaboration: Azure AD, Okta, Intune, OneDrive, Box, Zoom.
Three FDA-approved drugs: LIVMARLI (maralixibat) for cholestatic pruritus in Alagille syndrome and PFIC; CHOLBAM (cholic acid) for bile acid synthesis disorders; CTEXLI (chenodiol) for cerebrotendinous xanthomatosis. Late-stage pipeline includes volixibat for primary sclerosing cholangitis.
Mirum Pharmaceuticals, Inc.'s technology stack, projects, and hiring signals are inferred from public hiring and company data — career pages, public listings, and company web presence — then clustered and de-duplicated. Figures are estimates that refresh over time. Read our full methodology →
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